Muscular Dystrophy Stem Cell Medical Reports
Summaries of published research on stem cell therapy for muscular dystrophy, each linking to the original study.
-
Stem Cell Research & Therapy · 2023-04-27
Immunomodulatory Amnion-Derived Mesenchymal Stromal Cells Preserve Muscle Function in a Mouse Model of Duchenne Muscular Dystrophy
Yuko Nitahara-Kasahara, Soya Nakayama, Koichi Kimura, Sho Yamaguchi, Yuko Kakiuchi, Chikako Nito, Masahiro Hayashi, Tomoyuki Nakaishi, Yasuyoshi Ueda, and Takashi Okada.
-
Stem Cells Translational Medicine · 2021-07-27
The Use of Umbilical Cord-Derived Mesenchymal Stem Cells in Patients With Muscular Dystrophies: Results From Compassionate Use in Real-Life Settings
Beata Świątkowska-Flis, Izabela Zdolińska-Malinowska, Dominika Sługocka, and Dariusz Boruczkowski.
-
Cellular and Molecular Life Sciences · 2025-10-11
Cell Therapy for Duchenne Muscular Dystrophy: Promises, Challenges, and Controversies
Agnieszka Łoboda and Józef Dulak.
-
The Lancet · 2026-07-29
Deramiocel Heart-Derived Cellular Therapy in Advanced Duchenne Muscular Dystrophy (HOPE-3): A Phase 3, Randomised, Double-Blind, Placebo-Controlled Trial
Craig M McDonald, Chet Villa, Jonathan H Soslow, Kati Maharry, Nathaniel Hogan, Michael Binks, Kevin C Berth, Kristi A Elliott, Michael Taylor, Kan N Hor, James Signorovich, Erik K Henricson, Han C Phan, Susan Apkon, Partha S Ghosh, Cuixia Tian, Aravindhan Veerapandiyan, Leigh Ramos-Platt, Katheryn Gambetta, Saunder M Bernes, Arun S Varadhachary, Susan T Iannaccone, Chamindra G Laverty, Seth J Perlman, Nancy E Bass, Kathryn Mosher, Russell J Butterfield, Katherine D Mathews, Rebecca J Scharf, Edward C Smith, Jane Anne Emerson, Eugenio Mercuri, Mark S Awadalla, Linda Marbán, and Eduardo Marbán, on behalf of the HOPE-3 Investigators.
-
Stem Cell Reviews and Reports · 2025-12-18
Long-Term Safety and Efficacy of Systemic DT-DEC01 Cell Therapy in Non-Ambulatory Duchenne Muscular Dystrophy Patients: A 24-Month Clinical Evaluation
Maria Siemionow, Grzegorz Biegański, Adam Niezgoda, Agnieszka Sobkowiak-Sobierajska, Jarosław Czarnota, Krzysztof Siemionow, Anna Ziemiecka, Katarzyna Bożyk, and Jacek Wachowiak.
-
The Lancet · 2022-03-12
Repeated Intravenous Cardiosphere-Derived Cell Therapy in Late-Stage Duchenne Muscular Dystrophy (HOPE-2): A Multicentre, Randomised, Double-Blind, Placebo-Controlled, Phase 2 Trial
Craig M McDonald, Eduardo Marbán, Suzanne Hendrix, Nathaniel Hogan, Rachel Ruckdeschel Smith, Michelle Eagle, Richard S Finkel, Cuixia Tian, Joanne Janas, Matthew M Harmelink, Arun S Varadhachary, Michael D Taylor, Kan N Hor, Oscar H Mayer, Erik K Henricson, Pat Furlong, Deborah D Ascheim, Siegfried Rogy, Paula Williams, Linda Marbán, and the HOPE-2 Study Group.
-
Journal of Clinical Neurology · 2025-01-01
Safety and Tolerability of Wharton's Jelly-Derived Mesenchymal Stem Cells for Patients With Duchenne Muscular Dystrophy: A Phase 1 Clinical Study
Jiwon Lee, Sang Eon Park, Mira Kim, Hyeongseop Kim, Jeong-Yi Kwon, Hong Bae Jeon, Jong Wook Chang, and Jeehun Lee.
-
2020-10-12
Stem cell therapy for muscular dystrophies
Stefano Biressi, Antonio Filareto, Thomas A. Rando
-
2013-09-10
A clinical study shows safety and efficacy of autologous bone marrow mononuclear cell therapy to improve quality of life in muscular dystrophy patients
Alok Sharma, Hemangi Sane, Prerna Badhe, Nandini Gokulchandran, Pooja Kulkarni, Mamta Lohiya, Hema Biju, V C Jacob
-
2018-10-26
Efficacy of stem cell therapy in ambulatory and nonambulatory children with Duchenne muscular dystrophy
Alper Dai, Osman Baspinar, Ahmet Yeşilyurt, Eda Sun, Çiğdem İnci Aydemir, Olga Nehir Öztel, Davut Unsal Capkan, Ferda Pinarli, Abdullah Agar, Erdal Karaöz
-
2015-07-08
Duchenne Muscular Dystrophy — Sienkiewicz et al.
Dorota Sienkiewicz, Wojciech Kulak, Bożena Okurowska-Zawada, Grażyna Paszko-Patej, Katarzyna Kawnik
-
2017-02-28
Eteplirsen in the treatment of Duchenne muscular dystrophy
Kenji Rowel Q Lim, Rika Maruyama, Toshifumi Yokota
-
2021-11-30
Gene Therapy for Duchenne Muscular Dystrophy
Nertiyan Elangkovan, George Dickson
-
2018-02-03
Diagnosis and management of Duchenne muscular dystrophy
Prof David J Birnkrant, Prof Katharine Bushby, Carla M Bann, Prof Susan D Apkon, Angela Blackwell, David Brumbaugh, Laura E Case, Prof Paula R Clemens, Stasia Hadjiyannakis, Shree Pandya, Natalie Street, Jean Tomezsko, Prof Kathryn R Wagner, Leanne M Ward
-
2015-10-07
Duchenne Muscular Dystrophy — Falzarano et al.
Maria Sofia Falzarano, Chiara Scotton, Chiara Passarelli, Alessandra Ferlini, Alessandra Ferlini
Speak with a patient representative
No obligation. We’ll review your situation and respond within 48 hours.
- Response within 48 hours from a patient representative.
- Confidential — your information stays with us.
- No cost, no obligation. We review your case and respond.
Answering patient inquiries since 2005. A medical evaluation follows once we have your completed medical questionnaire.
