Muscular Dystrophy: Patient-reported outcomes
Patient-reported outcomes after stem cell therapy for Muscular Dystrophy, based on 52 patients in our follow-up registry.
Updated ·
Overall patient-reported outcomes
Physical condition
reported physical improvement
82%
N = 51
Quality of life
reported quality-of-life improvement
84%
N = 49
Treatment satisfaction
satisfied with the treatment outcome
77%
N = 51
Reported change vs. before treatment
Worse
No change
Small
Moderate
Significant
| Symptom | Reported change vs. before treatment | Reported improvement |
|---|---|---|
| Body pain |
|
85% |
| Muscle stiffness |
|
83% |
| Heart palpitations or arrhythmias |
|
79% |
| Muscle cramps |
|
77% |
| Difficulty swallowing |
|
73% |
| Enlarged muscles |
|
73% |
| Development delay (children) |
|
71% |
| Falls |
|
70% |
| Loss of muscle mass |
|
70% |
| Walking |
|
68% |
| Slurred speech |
|
67% |
| Standing up |
|
63% |
| Excessive sleeping or sleepiness |
|
58% |
| Behaviour problems (children) |
|
53% |
| Cognitive impairment |
|
46% |
| Walking up stairs |
|
42% |
| Droopy eye lids |
|
40% |
About this data
Patients self-assess each symptom on a 5-point scale (Worse / No improvement / Small / Moderate / Significant) at follow-up checkpoints after treatment, comparing to their pre-treatment baseline. "Reported improvement" combines the small, moderate and significant buckets. Data is updated daily from our internal patient registry. As with any medical treatment, past results do not guarantee future outcomes — improvements vary from patient to patient.
